"Familial renal amyloidosis"

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                            1
                            2020Medscape
                            Familial Renal Amyloidosis Familial Renal Amyloidosis: Practice Essentials, Background, Pathophysiology For YouNews & PerspectiveDrugs & DiseasesCME & EducationAcademyVideoDecision PointEdition:EnglishMedscapeEnglishDeutschEspañolFrançaisPortuguêsUKNewUnivadisLog In Sign Up It's Free!English EditionMedscape * English * Deutsch * Español * Français * Português * UKNewUnivadisXUnivadis from =aHR0cHM6Ly9lbWVkaWNpbmUubWVkc2NhcGUuY29tL2FydGljbGUvMjQ2MjIxLW92ZXJ2aWV3processing....Drugs & Diseases > Nephrology Familial Renal AmyloidosisUpdated: May 14, 2020 * Author: Helen J Lachmann, MD, MRCP; Chief Editor: Vecihi Batuman, MD, FASN more... * * Share * Email * Print * FeedbackClose * Facebook * Twitter * LinkedIn * WhatsAppSections Familial Renal Amyloidosis * * Sections Familial Renal Amyloidosis * Overview * * * Practice Essentials * Background
                            2
                            2019BMC Nephrology
                            Hereditary renal amyloidosis with a variant lysozyme p.Trp82Arg in a Chinese family: case report and literature review. Lysozyme amyloidosis is a rare hereditary systemic amyloidosis with amyloid deposits in various tissues leading to progressive organ failure. It has been mainly reported in developed countries since 1993. Here we report a lysozyme amyloidosis family with variant lysozyme
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                            3
                            2019BMC Nephrology
                            Typing of hereditary renal amyloidosis presenting with isolated glomerular amyloid deposition. The commonly used methods for amyloid typing include immunofluorescence or immunohistochemistry (IHC), which sometimes may come with diagnostic pitfalls. Mass spectrometry (MS)-based proteomics has been recognized as a reliable technique in amyloid typing. We reported two middle-aged patients who
                            4
                            2017Kidney international reports
                            Hereditary Renal Amyloidosis Associated With a Novel Apolipoprotein A-II Variant
                            5
                            2013Clinical kidney journal
                            Hereditary renal amyloidosis caused by a heterozygous G654A gelsolin mutation: a report of two cases Finnish-type familial amyloidosis (FAF) is a rare hereditary systemic amyloidosis that mainly exhibits cranial neuropathy. We describe a Japanese family with FAF manifested predominantly as renal amyloidosis. The proband was a 42-year-old woman with a 21-year history of proteinuria due to renal
                            6
                            2014British Committee for Standards in Haematology
                            Trip Score
                            NarrativeNarrative based
                            EvidenceEvidence based
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                            or FGG , clustered within specific functional domains (Haverkate & Samama, ; Miesbach et al , ; Shapiro et al , ). Some FGA variations cause hereditary renal amyloidosis, which is not associated with abnormal haemostasis (Gillmore et al , ). Afibrinogenaemia and hypofibrinogenaemia Clinical features In 106 cases with afibrinogenaemia or hypofibrinogenaemia in US, Iranian and Indian registries, the most
                            7
                            2014United Kingdom Haemophilia Centre Doctors' Organisation
                            Trip Score
                            NarrativeNarrative based
                            EvidenceEvidence based
                            ?
                            ; Shapiro et al, 2013). Some FGA variations cause hereditary renal amyloidosis, which is not associated with abnormal haemostasis (Gillmore et al, 2009). A?brinogenaemia and hypo?brinogenaemia Clinical features. In 106 cases with a?brinogenaemia or hypo?brinogenaemia in US, Iranian and Indian registries, the most common symptoms were mucocutaneous, soft-tis- sue, joint, genitourinary, traumatic
                            8
                            deficiencies (hypofibrinogenemia, hypo-dysfibrinogenemia, dysfibrinogenemia) and for more rare conditions, such as fibrinogen storage disease and hereditary renal amyloidosis. Instead, biallelic mutations have been associated with afibrinogenemia/severe hypofibrinogenemia, i.e., the severest forms of fibrinogen deficiency, affecting approximately 1-2 cases per million people. However, the "true" prevalence
                            9
                            2016Kidney international reports
                            Renal Amyloidosis Associated With 5 Novel Variants in the Fibrinogen A Alpha Chain Protein Fibrinogen A alpha chain amyloidosis is an autosomal dominant disease associated with mutations in the fibrinogen A alpha chain () gene, and it is the most common cause of hereditary renal amyloidosis in the UK. Patients typically present with kidney impairment and progress to end-stage renal disease over
                            10
                            2014eMedicine Pediatrics
                            . This website also contains material copyrighted by 3rd parties.Close encoded search term (Inherited Abnormalities of Fibrinogen) and Inherited Abnormalities of Fibrinogen What to Read Next on Medscape Related Conditions and Diseases * Inherited Abnormalities of Fibrinogen * Dysfibrinogenemia * Nonplatelet Hemostatic Disorders * Glanzmann Thrombasthenia * Thrombasthenia * Familial Renal Amyloidosis * Genetics of Glycogen-Storage Disease Type IV Medscape Consult News & Perspective * Diffuse Prothrombotic Syndrome After ChAdOx1 nCoV-19 Vaccine Administration * A Case of Chronic Thrombocytopenia in a 17-Year-Old Female * ACOG Updates Recommendations on Postpartum Hemorrhage Tools * Drug Interaction Checker * Pill Identifier * Calculators * FormularyRecommended * 2002960677
                            11
                            2014eMedicine Pediatrics
                            ) and Inherited Abnormalities of Fibrinogen What to Read Next on Medscape Related Conditions and Diseases * Inherited Abnormalities of Fibrinogen * Dysfibrinogenemia * Nonplatelet Hemostatic Disorders * Glanzmann Thrombasthenia * Thrombasthenia * Familial Renal Amyloidosis * Genetics of Glycogen-Storage Disease Type IV Medscape Consult News & Perspective * Diffuse Prothrombotic Syndrome After
                            12
                            2014eMedicine.com
                            on Medscape Related Conditions and Diseases * Amyloidosis * Macular Amyloidosis * Cardiac Amyloidosis * Transthyretin-Related Amyloidosis * AA (Inflammatory) Amyloidosis * Lichen Amyloidosis * Familial Renal Amyloidosis Medscape Consult News & Perspective * FDA OKs Vutrisiran for hATTR Amyloidosis With Polyneuropathy * Adequate Antibody Response to COVID-19 Vaccine in Patients
                            13
                            2014eMedicine.com
                            (Inflammatory) Amyloidosis * Lichen Amyloidosis * Familial Renal Amyloidosis Medscape Consult News & Perspective * FDA OKs Vutrisiran for hATTR Amyloidosis With Polyneuropathy * Adequate Antibody Response to COVID-19 Vaccine in Patients With Monoclonal Gammopathies and Light Chain Amyloidosis * New Tool Detects Difficult-to-Diagnose Cardiac Conditions Tools * Drug Interaction Checker * Pill
                            14
                            2014eMedicine Pediatrics
                            . This website also contains material copyrighted by 3rd parties.Close encoded search term (Inherited Abnormalities of Fibrinogen) and Inherited Abnormalities of Fibrinogen What to Read Next on Medscape Related Conditions and Diseases * Inherited Abnormalities of Fibrinogen * Dysfibrinogenemia * Nonplatelet Hemostatic Disorders * Glanzmann Thrombasthenia * Thrombasthenia * Familial Renal Amyloidosis * Genetics of Glycogen-Storage Disease Type IV Medscape Consult News & Perspective * Diffuse Prothrombotic Syndrome After ChAdOx1 nCoV-19 Vaccine Administration * A Case of Chronic Thrombocytopenia in a 17-Year-Old Female * ACOG Updates Recommendations on Postpartum Hemorrhage Tools * Drug Interaction Checker * Pill Identifier * Calculators * FormularyRecommended * 2002960677
                            15
                            2014eMedicine Pediatrics
                            . This website also contains material copyrighted by 3rd parties.Close encoded search term (Inherited Abnormalities of Fibrinogen) and Inherited Abnormalities of Fibrinogen What to Read Next on Medscape Related Conditions and Diseases * Inherited Abnormalities of Fibrinogen * Dysfibrinogenemia * Nonplatelet Hemostatic Disorders * Glanzmann Thrombasthenia * Thrombasthenia * Familial Renal Amyloidosis * Genetics of Glycogen-Storage Disease Type IV Medscape Consult News & Perspective * Diffuse Prothrombotic Syndrome After ChAdOx1 nCoV-19 Vaccine Administration * A Case of Chronic Thrombocytopenia in a 17-Year-Old Female * ACOG Updates Recommendations on Postpartum Hemorrhage Tools * Drug Interaction Checker * Pill Identifier * Calculators * FormularyRecommended * 2002960677
                            16
                            2014eMedicine.com
                            * Neutrophilia * Paroxysmal Cold Hemoglobinuria * Splenomegaly * Systemic MastocytosisLymphoproliferative Disorders * Burkitt Lymphoma and Burkitt-like Lymphoma * Castleman DiseasePlasma Cell Disorders * Familial Renal Amyloidosis * Gamma Heavy Chain Disease * Immunoglobulin-Related Amyloidosis * Light Chain-Associated Renal Disorders * Light-Chain Deposition Disease * Monoclonal Gammopathies of Undetermined Lymphoma (DLBCL) * Disseminated Intravascular Coagulation (DIC) * Dysfibrinogenemia * Eosinophilia * Erythroleukemia * Erythromelalgia * Esophageal Hematoma * Essential Thrombocytosis * Factor II Deficiency * Factor IX Deficiency (Hemophilia B) * Factor V Deficiency * Factor VII Deficiency * Factor X Deficiency * Factor XI Deficiency * Factor XIII Deficiency * Familial Renal Amyloidosis * Folate
                            17
                            2014eMedicine.com
                            * Neutrophilia * Paroxysmal Cold Hemoglobinuria * Splenomegaly * Systemic MastocytosisLymphoproliferative Disorders * Burkitt Lymphoma and Burkitt-like Lymphoma * Castleman DiseasePlasma Cell Disorders * Familial Renal Amyloidosis * Gamma Heavy Chain Disease * Immunoglobulin-Related Amyloidosis * Light Chain-Associated Renal Disorders * Light-Chain Deposition Disease * Monoclonal Gammopathies of Undetermined Lymphoma (DLBCL) * Disseminated Intravascular Coagulation (DIC) * Dysfibrinogenemia * Eosinophilia * Erythroleukemia * Erythromelalgia * Esophageal Hematoma * Essential Thrombocytosis * Factor II Deficiency * Factor IX Deficiency (Hemophilia B) * Factor V Deficiency * Factor VII Deficiency * Factor X Deficiency * Factor XI Deficiency * Factor XIII Deficiency * Familial Renal Amyloidosis * Folate
                            18
                            2014eMedicine.com
                            * Macular Amyloidosis * Cardiac Amyloidosis * Transthyretin-Related Amyloidosis * AA (Inflammatory) Amyloidosis * Lichen Amyloidosis * Familial Renal Amyloidosis Medscape Consult News & Perspective * FDA OKs Vutrisiran for hATTR Amyloidosis With Polyneuropathy * Adequate Antibody Response to COVID-19 Vaccine in Patients With Monoclonal Gammopathies and Light Chain Amyloidosis * New Tool
                            19
                            2014eMedicine.com
                            (Inflammatory) Amyloidosis * Lichen Amyloidosis * Familial Renal Amyloidosis Medscape Consult News & Perspective * FDA OKs Vutrisiran for hATTR Amyloidosis With Polyneuropathy * Adequate Antibody Response to COVID-19 Vaccine in Patients With Monoclonal Gammopathies and Light Chain Amyloidosis * New Tool Detects Difficult-to-Diagnose Cardiac Conditions Tools * Drug Interaction Checker * Pill
                            20
                            2014eMedicine.com
                            Amyloidosis What to Read Next on Medscape Related Conditions and Diseases * Amyloidosis * Macular Amyloidosis * Cardiac Amyloidosis * Transthyretin-Related Amyloidosis * AA (Inflammatory) Amyloidosis * Lichen Amyloidosis * Familial Renal Amyloidosis Medscape Consult News & Perspective * FDA OKs Vutrisiran for hATTR Amyloidosis With Polyneuropathy * Adequate Antibody Response to COVID-19